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<jats:p>Effective treatment of spinal muscular atrophy with antisense oligonucleotide therapy opens the door to treating other neurological disorders with this approach.</jats:p>

Original publication

DOI

10.1126/scitranslmed.aay2069

Type

Journal article

Journal

Science Translational Medicine

Publisher

American Association for the Advancement of Science (AAAS)

Publication Date

25/09/2019

Volume

11

Pages

eaay2069 - eaay2069