Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR

Cehajic-Kapetanovic J., Xue K., Martinez-Fernandez de la Camara C., Nanda A., Davies A., Wood LJ., Salvetti AP., Fischer MD., Aylward JW., Barnard AR., Jolly JK., Luo E., Lujan BJ., Ong T., Girach A., Black GCM., Gregori NZ., Davis JL., Rosa PR., Lotery AJ., Lam BL., Stanga PE., MacLaren RE.

DOI

10.1038/s41591-020-0763-1

Type

Journal article

Journal

Nature Medicine

Publisher

Springer Science and Business Media LLC

Publication Date

03/2020

Volume

26

Pages

354 - 359

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