Beneficial effects on vision in patients undergoing retinal gene therapy for choroideremia

Xue K., Jolly JK., Barnard AR., Rudenko A., Salvetti AP., Patrício MI., Edwards TL., Groppe M., Orlans HO., Tolmachova T., Black GC., Webster AR., Lotery AJ., Holder GE., Downes SM., Seabra MC., MacLaren RE.

DOI

10.1038/s41591-018-0185-5

Type

Journal article

Journal

Nature Medicine

Publisher

Springer Science and Business Media LLC

Publication Date

10/2018

Volume

24

Pages

1507 - 1512

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