A Quantitative Chloride Channel Conductance Assay for Efficacy Testing of AAV.BEST1

Wood SR., McClements ME., Martinez-Fernandez de la Camara C., Patrício MI., Uggenti C., Sekaran S., Barnard AR., Manson FD., MacLaren RE.

DOI

10.1089/hgtb.2018.267

Type

Journal article

Journal

Human Gene Therapy Methods

Publisher

Mary Ann Liebert Inc

Publication Date

04/2019

Volume

30

Pages

44 - 52

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