IMPG2-associated retinal dystrophy with a novel missense variant and therapeutic options via adenine base editing

Abdalla Elsayed MEA., Barone V., Kaukonen M., Raybould MIJ., MacLaren RE.

DOI

10.1080/13816810.2025.2609679

Type

Journal article

Publisher

Informa UK Limited

Publication Date

2026-03-04T00:00:00+00:00

Volume

47

Pages

172 - 178

Total pages

6

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