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IMPG2-associated retinal dystrophy with a novel missense variant and therapeutic options via adenine base editing
Abdalla Elsayed MEA., Barone V., Kaukonen M., Raybould MIJ., MacLaren RE.
DOI
10.1080/13816810.2025.2609679
Type
Journal article
Publisher
Informa UK Limited
Publication Date
2026-01-01T00:00:00+00:00
Pages
1 - 7
Total pages
6