Codon-Optimized RPGR Improves Stability and Efficacy of AAV8 Gene Therapy in Two Mouse Models of X-Linked Retinitis Pigmentosa

Fischer MD., McClements ME., Martinez-Fernandez de la Camara C., Bellingrath J-S., Dauletbekov D., Ramsden SC., Hickey DG., Barnard AR., MacLaren RE.

DOI

10.1016/j.ymthe.2017.05.005

Type

Journal article

Publisher

Elsevier BV

Publication Date

2017-08-01T00:00:00+00:00

Volume

25

Pages

1854 - 1865

Total pages

11

Permalink More information Close