Retinal Gene Therapy in X-Linked Retinitis Pigmentosa Caused by Mutations in RPGR: Results at 6 Months in a First in Human Clinical Trial

Cehajic-Kapetanovic J., Xue K., de la Camara CM-F., Nanda A., Davies A., Wood LJ., Salvetti AP., Fischer DM., Aylward JW., Barnard AR., Jolly JK., Luo E., Lujan BJ., Ong T., Girach A., Black GCM., Gregori NZ., Davis JL., Rosa PR., Lotery AJ., Lam BL., Stanga PE., MacLaren RE.

Type

Conference paper

Publication Date

2020

Volume

28

Pages

1 - 1

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