A GAA repeat expansion reporter model of Friedreich's ataxia recapitulates the genomic context and allows rapid screening of therapeutic compounds

Lufino MMP., Silva AM., Nemeth AH., Alegre-Abarrategui J., Russell AJ., Wade-Martins R.

DOI

10.1093/hmg/ddt370

Type

Journal article

Journal

Human Molecular Genetics

Publisher

Oxford University Press (OUP)

Publication Date

20/12/2013

Volume

22

Pages

5173 - 5187

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