Single residue AAV capsid mutation improves transduction of photoreceptors in the Abca4−/− mouse and bipolar cells in the rd1 mouse and human retina ex vivo

De Silva SR., Charbel Issa P., Singh MS., Lipinski DM., Barnea-Cramer AO., Walker NJ., Barnard AR., Hankins MW., MacLaren RE.

DOI

10.1038/gt.2016.54

Type

Journal article

Journal

Gene Therapy

Publisher

Springer Science and Business Media LLC

Publication Date

11/2016

Volume

23

Pages

767 - 774

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