Search results (82)
« Back to PublicationsInvestigating ethnicity-related variability in the human L-cone spectral sensitivity function
Journal article
Schneider AC. et al, (2026), Vision Research, 243, 108769 - 108769
Gene Therapy Strategies for the Treatment of Bestrophinopathies.
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Haldrup SB. et al, (2025), Int J Mol Sci, 26
CRISPR targeting of SNPs associated with age-related macular degeneration in ARPE-19 cells: a potential model for manipulating the complement system
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Salman A. et al, (2025), Gene Therapy, 32, 132 - 141
Comparison of CRISPR-Cas13b RNA base editing approaches for USH2A-associated inherited retinal degeneration
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Fry LE. et al, (2025), Communications Biology, 8
Gene Therapies in Clinical Development to Treat Retinal Disorders
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McClements ME. et al, (2024), Molecular Diagnosis & Therapy, 28, 575 - 591
Genetic therapies and potential therapeutic applications of CRISPR activators in the eye.
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Ng BW. et al, (2024), Prog Retin Eye Res, 102
Single-cell transcriptomic analysis of retinal immune regulation and blood-retinal barrier function during experimental autoimmune uveitis
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Quinn J. et al, (2024), Scientific Reports, 14
Rescue of cone and rod photoreceptor function in a CDHR1-model of age-related retinal degeneration
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Yusuf IH. et al, (2024), Molecular Therapy, 32, 1445 - 1460
CRISPR Manipulation of Age-Related Macular Degeneration Haplotypes in the Complement System: Potential Future Therapeutic Applications/Avenues
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Salman A. et al, (2024), International Journal of Molecular Sciences, 25, 1697 - 1697
Programmable RNA editing with endogenous ADAR enzymes – a feasible option for the treatment of inherited retinal disease?
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Bellingrath J-S. et al, (2023), Frontiers in Molecular Neuroscience, 16
A Review of CRISPR Tools for Treating Usher Syndrome: Applicability, Safety, Efficiency, and In Vivo Delivery.
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Major L. et al, (2023), Int J Mol Sci, 24
Erratum: Enhancement of Adeno-Associated Virus-Mediated Gene Therapy Using Hydroxychloroquine in Murine and Human Tissues.
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Chandler LC. et al, (2023), Mol Ther Methods Clin Dev, 28
Future Perspectives of Prime Editing for the Treatment of Inherited Retinal Diseases.
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Hansen S. et al, (2023), Cells, 12
Impaired glutamylation of RPGR ORF15 underlies the cone-dominated phenotype associated with truncating distal ORF15 variants
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Cehajic-Kapetanovic J. et al, (2022), Proceedings of the National Academy of Sciences, 119